Kolexia
Semeraro Michaela Pédiatrie
Semeraro Michaela
Pédiatrie
Hôpital Necker Enfants Malades
Paris, France
90 Activités
99 Followers
Scientifique
Digital
Production scientifique
Activités par an
Expertise
Sujets de recherche
{{person.topmesh1.name}} Thalassémie Drépanocytose Bêta-Thalassémie Anémie Syndrome de Wiskott-Aldrich Hémoglobinopathies Maladies d'immunodéficience primaire Fibrose Récidive tumorale locale

Collaborateurs

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Cavazzana Marina
Cavazzana Marina
Hôpital Necker Enfants Malades, Paris, France
Magrin Elisa
Magrin Elisa
Hôpital Necker Enfants Malades, Paris, France
Magnani Alessandra
Magnani Alessandra
Hôpital Necker Enfants Malades, Paris, France
Zitvogel Laurence
Zitvogel Laurence
Gustave-Roussy, Villejuif, France

Industries

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Vertex
6 collaboration(s)
Dernière en 2023
PHARMING GROUP N.V.
4 collaboration(s)
Dernière en 2023
Creativ-Ceutical SARL
3 collaboration(s)
Dernière en 2023
AXELYS SANTE
2 collaboration(s)
Dernière en 2020

Dernières activités

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A Study to Assess Safety, Pharmacokinetics, and Pharmacodynamics of mRNA-3705 in Participants With Isolated Methylmalonic Acidemia: A Global, Phase 1/2, Open-Label, Dose Optimization Study to Evaluate the Safety, Tolerability, Pharmacodynamics, and Pharmacokinetics of mRNA-3705 in Participants With Isolated Methylmalonic Acidemia Due to Methylmalonyl-CoA Mutase Deficiency
Essai Clinique (ModernaTX, Inc.)   15 mars 2024
Lumacaftor/Ivacaftor Population Pharmacokinetics in Pediatric Patients with Cystic Fibrosis: A First Step Toward Personalized Therapy.
Clinical pharmacokinetics   04 février 2024
Long-term Follow-up of Subjects With Sickle Cell Disease Treated With Ex Vivo Gene Therapy Using Autologous Hematopoietic Stem Cells Transduced With a Lentiviral Vector
Essai Clinique (Bluebird)   08 janvier 2024
Long-term neurological and neurodevelopmental outcome of neonatal listeriosis in France: a prospective, matched, observational cohort study.
The Lancet. Child & adolescent health   20 octobre 2023
Long-term Follow-up of Subjects With Transfusion-Dependent β-Thalassemia (TDT) Treated With Ex Vivo Gene Therapy Using Autologous Hematopoietic Stem Cells Transduced With a Lentiviral Vector
Essai Clinique (Bluebird)   13 octobre 2023
Immunologie
Compte-rendu du Congrès de la Société Française de Pédiatrie 2023   01 septembre 2023
Santé des migrants mineurs
Compte-rendu du Congrès de la Société Française de Pédiatrie 2023   01 septembre 2023
Sickle Cell Disease: From Genetics to Curative Approaches.
Annual review of genomics and human genetics   28 août 2023
Activated phosphoinositide 3-kinase δ syndrome: Update from the ESID Registry and comparison with other autoimmune-lymphoproliferative inborn errors of immunity.
The Journal of allergy and clinical immunology   28 juin 2023
Study to Determine the Safety and Tolerability of Sotatercept (ACE-011) in Adults With Beta( β)- Thalassemia.: A Phase 2A, Open-label Dose Finding Study to Determine the Safety and Tolerability of Sotatercept (ACE-011) in Adults With BETA(b)-THALASSEMIA.
Essai Clinique (Celgene)   23 mai 2023